The patient’s view on rare disease trial design – a qualitative study

The patient’s view on rare disease trial design – a qualitative study

Abstract Background Clinical trials in rare diseases are more challenging than trials in frequent diseases. Small numbers of eligible trial participants, often complicated by heterogeneity among rare disease patients, hamper the design and conduct of a ‘classical’ Randomized Controlled Trial. Theref...

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Bibliographic Details
Main Authors: C. M. W. Gaasterland, M. C. Jansen – van der Weide, M. J. du Prie – Olthof, M. Donk, M. M. Kaatee, R. Kaczmarek, C. Lavery, K. Leeson-Beevers, N. O’Neill, O. Timmis, V. van Nederveen, E. Vroom, J. H. van der Lee
Format: Article
Language:English
Published: BMC 2019-02-01
Series:Orphanet Journal of Rare Diseases
Subjects:
Rare diseases
Patient involvement
Qualitative study
Online Access:http://link.springer.com/article/10.1186/s13023-019-1002-z

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http://link.springer.com/article/10.1186/s13023-019-1002-z

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