P005: Head-to-head trial of pegunigalsidase alfa vs agalsidase beta in Fabry disease: Phase 3 randomized, double-blind, BALANCE Study 2-year results
Main Authors: | , , , , , , , , , , , , , , , , , , , , , , , , , , , , , , , |
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Format: | Article |
Jezik: | English |
Izdano: |
Elsevier
2023-01-01
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Serija: | Genetics in Medicine Open |
Online dostop: | http://www.sciencedirect.com/science/article/pii/S2949774423000158 |