Delivery strategies for CRISPR/Cas genome editing tool for retinal dystrophies: challenges and opportunities

CRISPR/Cas, an adaptive immune system in bacteria, has been adopted as an efficient and precise tool for site-specific gene editing with potential therapeutic opportunities. It has been explored for a variety of applications, including gene modulation, epigenome editing, diagnosis, mRNA editing, etc...

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Bibliographic Details
Main Authors: Aayushi Lohia, Deepak Kumar Sahel, Mohd Salman, Vivek Singh, Indumathi Mariappan, Anupama Mittal, Deepak Chitkara
Format: Article
Language:English
Published: Elsevier 2022-03-01
Series:Asian Journal of Pharmaceutical Sciences
Subjects:
Online Access:http://www.sciencedirect.com/science/article/pii/S1818087622000149