Lung Inflammatory Genes in Cystic Fibrosis and Their Relevance to Cystic Fibrosis Transmembrane Conductance Regulator Modulator Therapies

Cystic fibrosis (CF) is a monogenic syndrome determined by over 2000 mutations in the <i>CF Transmembrane Conductance Regulator</i> (<i>CFTR</i>) gene harbored on chromosome 7. In people with CF (PWCF), lung disease is the major determinant of morbidity and mortality and is c...

Full description

Bibliographic Details
Main Authors: Annalucia Carbone, Pamela Vitullo, Sante Di Gioia, Massimo Conese
Format: Article
Language:English
Published: MDPI AG 2023-10-01
Series:Genes
Subjects:
Online Access:https://www.mdpi.com/2073-4425/14/10/1966