Quality of Life with Late-Onset Pompe Disease: Qualitative Interviews and General Public Utility Estimation in the United Kingdom

Quality of Life with Late-Onset Pompe Disease: Qualitative Interviews and General Public Utility Estimation in the United Kingdom

**Background:** Late-onset Pompe disease (LOPD) is a rare, progressive neuromuscular condition typically characterized by weakness of skeletal muscles, including those involved in respiration and diaphragmatic dysfunction. Individuals with LOPD typically eventually require mobility and/or ventilator...

Full description

Bibliographic Details
Main Authors: Lena Hubig, Anna-Katrine Sussex, Alasdair MacCulloch, Derralynn Hughes, Ryan Graham, Liz Morris, Syed Raza, Andrew J. Lloyd, Amanda Sowinski, Katy Gallop
Format: Article
Language:English
Published: Columbia Data Analytics, LLC 2023-03-01
Series:Journal of Health Economics and Outcomes Research
Online Access:https://doi.org/10.36469/001c.68157

Internet

https://doi.org/10.36469/001c.68157

Similar Items