Profiling trial burden and patients’ attitudes to improve clinical research in epidermolysis bullosa

Profiling trial burden and patients’ attitudes to improve clinical research in epidermolysis bullosa

Abstract Background Epidermolysis bullosa (EB) comprises inherited mechanobullous dermatoses with considerable morbidity and mortality. While current treatments are symptomatic, a growing number of innovative therapeutic compounds are evaluated in clinical trials. Clinical research in rare diseases...

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Bibliographic Details
Main Authors: Christine Prodinger, Anja Diem, Katherina Ude-Schoder, Josefina Piñón-Hofbauer, Sophie Kitzmueller, Johann W. Bauer, Martin Laimer
Format: Article
Language:English
Published: BMC 2020-07-01
Series:Orphanet Journal of Rare Diseases
Subjects:
Epidermolysis bullosa
Clinical trial
Rare disease
Recruitment failures
Challenges for trial design
Online Access:http://link.springer.com/article/10.1186/s13023-020-01443-3

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http://link.springer.com/article/10.1186/s13023-020-01443-3

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