Engineering CRISPR for emerging therapeutic applications

Clustered regularly interspaced short palindromic repeats (CRISPRs) were originally identified in bacterial and archaeal genomes as an adaptive immune response against invading viruses and phages. The discovery of the ability of CRISPR–Cas9 to cut targeted DNA sequences at predetermined sites has in...

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Bibliographic Details
Main Authors: Xiaoqi Sun, Zhuang Liu
Format: Article
Language:English
Published: Elsevier 2024-12-01
Series:EngMedicine
Subjects:
Online Access:http://www.sciencedirect.com/science/article/pii/S2950489924000356