Development of a novel PRO instrument for use in familial chylomicronemia syndrome

Development of a novel PRO instrument for use in familial chylomicronemia syndrome

Abstract Background Familial chylomicronemia syndrome (FCS), a rare genetic disorder characterized by high levels of circulating triglycerides, negatively impacts multiple organs, including the liver and pancreas. Objective The objective of this study was to develop and support the content validity...

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Bibliographic Details
Main Authors: David Davidson, Christina Slota, Montserrat Vera-Llonch, T. Michelle Brown, Andrew Hsieh, Sheri Fehnel
Format: Article
Language:English
Published: SpringerOpen 2021-08-01
Series:Journal of Patient-Reported Outcomes
Subjects:
Familial chylomicronemia syndrome
Patient-reported outcomes
PRO measure
FCS Symptoms and Impacts Scale
Clinical outcome assessment
COA
Online Access:https://doi.org/10.1186/s41687-021-00347-5

Internet

https://doi.org/10.1186/s41687-021-00347-5

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