Current status and developments in gene therapy for thalassemia and sickle cell disease
β-thalassemias and sickle cell anemia (SCA) are the most common monogenic diseases worldwide for which curative treatments remain a desired goal. Allogeneic hematopoietic stem cell transplantation (allo-HCT), - the only curative treatment currently available for hemoglobinopaties-, has a narrow appl...
| Main Authors: | , |
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| Format: | Article |
| Language: | English |
| Published: |
MDPI AG
2014-12-01
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| Series: | Thalassemia Reports |
| Subjects: | |
| Online Access: | http://www.pagepressjournals.org/index.php/thal/article/view/4876 |