Improvements with burosumab treatment in an early access programme for adults with X-linked hypophosphataemia: A case series of three patients
X-linked hypophosphataemia (XLH) is a life-long phosphate-wasting disorder that causes skeletal deformities, pain, stiffness, and fatigue and impairs quality of life. Burosumab was approved for use in adults in 2020. We describe three adults with persistent XLH symptoms who received burosumab treatm...
| Glavni autori: | , , |
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| Format: | Članak |
| Jezik: | English |
| Izdano: |
Elsevier
2024-12-01
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| Serija: | Bone Reports |
| Teme: | |
| Online pristup: | http://www.sciencedirect.com/science/article/pii/S2352187224000810 |