Gene therapy in haemophilia: literature review and regional perspectives for Turkey

Haemophilia is an X-linked lifelong congenital bleeding disorder that is caused by insufficient levels of factor VIII (FVIII; haemophilia A) or factor IX (FIX; haemophilia B) and characterized by spontaneous and trauma-related bleeding episodes. The cornerstone of the treatment, factor replacement,...

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Bibliographic Details
Main Authors: Kaan Kavaklı, Bülent Antmen, Vahap Okan, Fahri Şahin, Selin Aytaç, Can Balkan, Ergül Berber, Zühre Kaya, Alphan Küpesiz, Bülent Zülfikar
Format: Article
Language:English
Published: SAGE Publishing 2022-07-01
Series:Therapeutic Advances in Hematology
Online Access:https://doi.org/10.1177/20406207221104591