Gene therapy in haemophilia: literature review and regional perspectives for Turkey
Haemophilia is an X-linked lifelong congenital bleeding disorder that is caused by insufficient levels of factor VIII (FVIII; haemophilia A) or factor IX (FIX; haemophilia B) and characterized by spontaneous and trauma-related bleeding episodes. The cornerstone of the treatment, factor replacement,...
Main Authors: | , , , , , , , , , |
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Format: | Article |
Language: | English |
Published: |
SAGE Publishing
2022-07-01
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Series: | Therapeutic Advances in Hematology |
Online Access: | https://doi.org/10.1177/20406207221104591 |