Correction : Long-term safety and clinical outcomes of olipudase alfa enzyme replacement therapy in pediatric patients with acid sphingomyelinase deficiency: two-year results

Bibliographic Details
Main Authors: George A. Diaz, Roberto Giugliani, Nathalie Gufon, Simon A. Jones, Eugen Mengel, Maurizio Scarpa, Peter Witters, Abhimanyu Yarramaneni, Jing Li, Nicole M. Armstrong, Yong Kim, Catherine Ortemann-Renon, Monica Kumar
Format: Article
Language:English
Published: BMC 2023-03-01
Series:Orphanet Journal of Rare Diseases
Online Access:https://doi.org/10.1186/s13023-023-02647-z