Motor function in type 2 and 3 SMA patients treated with Nusinersen: a critical review and meta-analysis
Abstract Background There is an increasing number of papers reporting the real world use of Nusinersen in different cohorts of SMA patients. Main body The aim of this paper was to critically review the literature reporting real world data on motor function in type 2 and 3 patients treated with Nusin...
| Auteurs principaux: | , , , , , , , , , , |
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| Format: | Article |
| Langue: | English |
| Publié: |
BMC
2021-10-01
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| Collection: | Orphanet Journal of Rare Diseases |
| Sujets: | |
| Accès en ligne: | https://doi.org/10.1186/s13023-021-02065-z |