Patient-reported burden of hereditary transthyretin amyloidosis on functioning and well-being

Patient-reported burden of hereditary transthyretin amyloidosis on functioning and well-being

Abstract Background Hereditary transthyretin (hATTR) amyloidosis is a rare, systemic, progressive, and life-threatening disease in which transthyretin proteins misfold and aggregate as insoluble amyloid deposits, disrupting nervous, cardiac, gastrointestinal, and other organ tissues. There are limit...

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Bibliographic Details
Main Authors: Andrew Lovley, Kimberly Raymond, Spencer D. Guthrie, Michael Pollock, Vaishali Sanchorawala, Michelle K. White
Format: Article
Language:English
Published: SpringerOpen 2021-01-01
Series:Journal of Patient-Reported Outcomes
Subjects:
Amyloidosis
Burden of disease
Quality of life
Patient interviews
Qualitative
Rare disease
Online Access:https://doi.org/10.1186/s41687-020-00273-y

Internet

https://doi.org/10.1186/s41687-020-00273-y

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