The clinical experience of compassionate use program for avapritinib: implications for drug positioning in the therapeutic scenario of systemic mastocytosis
In systemic mastocytosis, cytoreductive treatment is indicated for advanced systemic mastocytosis (AdvSM) variants. The treatment scenario is rapidly diversifying especially with the introduction of KIT tyrosine kinase inhibitors. Avapritinib is a second-generation potent and selective inhibitor of...
Main Authors: | , , , , , , , , , , |
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Format: | Article |
Language: | English |
Published: |
SAGE Publishing
2023-10-01
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Series: | Therapeutic Advances in Hematology |
Online Access: | https://doi.org/10.1177/20406207231205643 |