Enteric-Coated Cysteamine Bitartrate in Cystinosis Patients

Enteric-Coated Cysteamine Bitartrate in Cystinosis Patients

Cystinosis is a severe inherited metabolic storage disease caused by the lysosomal accumulation of cystine. Lifelong therapy with the drug cysteamine bitartrate is necessary. Cysteamine cleaves intralysosomal cystine, and thereafter, it can exit from the organelle. The need for frequent dosing every...

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Bibliographic Details
Main Authors: Sabrina Klank, Christina van Stein, Marianne Grüneberg, Chris Ottolenghi, Kerstin K. Rauwolf, Jürgen Grebe, Janine Reunert, Erik Harms, Thorsten Marquardt
Format: Article
Language:English
Published: MDPI AG 2023-06-01
Series:Pharmaceutics
Subjects:
cystinosis
enteric-coated cysteamine
immediate-release cysteamine (Cystagon<sup>®</sup>)
cystine-levels
pharmacokinetics
Online Access:https://www.mdpi.com/1999-4923/15/7/1851

Internet

https://www.mdpi.com/1999-4923/15/7/1851

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