Reinstitution of pegvaliase therapy during lactation

Pegvaliase, an injectable form of phenylalanine ammonia lyase, is an enzyme substitution therapy for adults with phenylketonuria (PKU). Experience with pegvaliase during lactation is scarce. Limited evidence suggests that pegvaliase does not pass into breast milk. The case presented here describes t...

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Bibliographic Details
Main Authors: Frances Rohr, Ann Wessel, Cary O. Harding, Susan E. Waisbren, Krista Viau, Amy Kritzer
Format: Article
Language:English
Published: Elsevier 2022-12-01
Series:Molecular Genetics and Metabolism Reports
Subjects:
Online Access:http://www.sciencedirect.com/science/article/pii/S2214426922000982