PB2064: THE COMPLETE STUDY: A SINGLE ARM, MULTICENTER OBSERVATIONAL STUDY TO EVALUATE EFFECTIVENESS OF PEGCETACOPLAN UNDER REAL WORLD CONDITIONS IN PATIENTS WITH PAROXYSMAL NOCTURNAL HEMOGLOBINURIA (PNH)

Detalles Bibliográficos
Main Authors: Régis Peffault de Latour, Jeff Szer, Austin Kulasekararaj, Anna Gaya, Simona Sica, Matthias Nölte, Regina Horneff, Lethagen Stefan
Formato: Artigo
Idioma:English
Publicado: Wiley 2023-08-01
Series:HemaSphere
Acceso en liña:http://journals.lww.com/10.1097/01.HS9.0000975056.36410.cc