REAL-WORLD DATA ON THE TREATMENT OF SICKLE CELL DISEASE WITH VOXELOTOR: RESULTS FROM A BRAZIL'S EARLY ACCESS PROGRAM
Introduction: Voxelotor, is a first-in-class modifying therapy approved to treat patients with sickle cell disease (SCD), a once-daily, oral treatment that reversibly binds to the a-chain of hemoglobin (Hb) and modulates its affinity for oxygen, inhibits Hb S polymerazation, preventing HbS sickling...
| Main Authors: | , , , , |
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| Format: | Article |
| Language: | English |
| Published: |
Elsevier
2023-10-01
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| Series: | Hematology, Transfusion and Cell Therapy |
| Online Access: | http://www.sciencedirect.com/science/article/pii/S2531137923003723 |