Catching Them Early: Framework Parameters and Progress for Prenatal and Childhood Application of Advanced Therapies

Catching Them Early: Framework Parameters and Progress for Prenatal and Childhood Application of Advanced Therapies

Advanced therapy medicinal products (ATMPs) are medicines for human use based on genes, cells or tissue engineering. After clear successes in adults, the nascent technology now sees increasing pediatric application. For many still untreatable disorders with pre- or perinatal onset, timely interventi...

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Bibliographic Details
Main Authors: Carsten W. Lederer, Lola Koniali, Tina Buerki-Thurnherr, Panayiota L. Papasavva, Stefania La Grutta, Amelia Licari, Frantisek Staud, Donato Bonifazi, Marina Kleanthous
Format: Article
Language:English
Published: MDPI AG 2022-04-01
Series:Pharmaceutics
Subjects:
gene therapy
somatic cell therapy
tissue-engineered medicinal product
CAR T cell
CAR NK cell
hematopoietic stem and progenitor cell
Online Access:https://www.mdpi.com/1999-4923/14/4/793

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https://www.mdpi.com/1999-4923/14/4/793

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