Renoprotective Effect of Agalsidase Alfa: A Long-Term Follow-Up of Patients with Fabry Disease

Renoprotective Effect of Agalsidase Alfa: A Long-Term Follow-Up of Patients with Fabry Disease

Fabry disease is a rare lysosomal storage disorder caused by mutations in the GLA gene, which, without treatment, can cause significant renal dysfunction. We evaluated the effects of enzyme replacement therapy with agalsidase alfa on renal decline in patients with Fabry disease using data from the F...

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Bibliographic Details
Main Authors: Markus Cybulla, Kathleen Nicholls, Sandro Feriozzi, Aleš Linhart, Joan Torras, Bojan Vujkovac, Jaco Botha, Christina Anagnostopoulou, Michael L. West
Format: Article
Language:English
Published: MDPI AG 2022-08-01
Series:Journal of Clinical Medicine
Subjects:
Fabry disease
proteinuria
estimated glomerular filtration rate
enzyme replacement therapy
Online Access:https://www.mdpi.com/2077-0383/11/16/4810

Internet

https://www.mdpi.com/2077-0383/11/16/4810

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