Real-world evidence of eteplirsen treatment effects in patients with Duchenne muscular dystrophy in the USA

Aim: To evaluate treatment effects of eteplirsen among patients with Duchenne muscular dystrophy. Methods: Using real-world claims and electronic medical record data, this retrospective comparative analysis assessed eteplirsen-treated and control cohorts matched by age, disease progression state,...

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Bibliographic Details
Main Authors: Joel Iff, Yi Zhon, Edward Tuttle, Deepshekhar Gupta, Xander Paul, Erik Henricson
Format: Article
Language:English
Published: Becaris Publishing Limited 2023-08-01
Series:Journal of Comparative Effectiveness Research
Subjects: