Stepwise shortening of agalsidase beta infusion duration in Fabry disease: Clinical experience with infusion rate escalation protocol

Abstract Background Although enzyme replacement therapy with agalsidase beta resulted in a variety of clinical benefits, life‐long biweekly intravenous infusion may impact on patients’ quality of life. Moreover, regular infusions are time‐consuming: although a stepwise shortening of infusion duratio...

Full description

Bibliographic Details
Main Authors: Eleonora Riccio, Mario Zanfardino, Monica Franzese, Ivana Capuano, Pasquale Buonanno, Lucia Ferreri, Maria Amicone, Antonio Pisani
Format: Article
Language:English
Published: Wiley 2021-05-01
Series:Molecular Genetics & Genomic Medicine
Subjects:
Online Access:https://doi.org/10.1002/mgg3.1659