Twice-Weekly Outpatient Rehabilitation Intervention for Young Children With Spinal Muscular Atrophy Treated With Genetic-Based Therapies: Protocol for a Feasibility Study

Twice-Weekly Outpatient Rehabilitation Intervention for Young Children With Spinal Muscular Atrophy Treated With Genetic-Based Therapies: Protocol for a Feasibility Study

BackgroundSpinal muscular atrophy (SMA) is a progressive neuromuscular disorder that causes muscle weakness and is the leading genetic cause of infant mortality worldwide. While no definitive cure exists, the approval of 3 genetic-based therapies in Canada since 2018 has led...

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Bibliographic Details
Main Authors: Christina Ippolito, Lathushikka Canthiya, Amanda Floreani, Kathleen Luckhart, Andrea Hoffman, Laura McAdam
Format: Article
Language:English
Published: JMIR Publications 2023-11-01
Series:JMIR Research Protocols
Online Access:https://www.researchprotocols.org/2023/1/e46363

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https://www.researchprotocols.org/2023/1/e46363

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