The Metreleptin Effectiveness and Safety Registry (MEASuRE): concept, design and challenges

The Metreleptin Effectiveness and Safety Registry (MEASuRE): concept, design and challenges

Abstract Background Metreleptin, a recombinant analog of human leptin, is an approved therapy, adjunct to diet, to treat the metabolic complications of leptin deficiency in patients with lipodystrophy – a group of rare diseases characterized by a paucity of adipose tissue. MEASuRE (Metreleptin Effec...

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Bibliographic Details
Main Authors: Morey W Haymond, David Araújo-Vilar, John Balser, James H Lewis, Ruth Louzado, Carla Musso, Julia von Schnurbein, Martin Wabitsch, on behalf of the MEASuRE group
Format: Article
Language:English
Published: BMC 2023-05-01
Series:Orphanet Journal of Rare Diseases
Subjects:
Lipodystrophy
Leptin
Metreleptin
Registry
Real-world data
Online Access:https://doi.org/10.1186/s13023-023-02714-5

Internet

https://doi.org/10.1186/s13023-023-02714-5

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