Disease progression rates in ambulatory Duchenne muscular dystrophy by steroid type, patient age and functional status
Aim: To examine benefits of corticosteroids for Duchenne muscular dystrophy (DMD) by age and disease progression. Methods: Data from daily steroid users (placebo-treated) were pooled from four phase 2b/3 trials in DMD. Outcomes assessed overall and among subgroups included changes from baseline to...
| Main Authors: | , , , , , , , , , , |
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| Format: | Article |
| Language: | English |
| Published: |
Becaris Publishing Limited
2023-02-01
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| Series: | Journal of Comparative Effectiveness Research |
| Subjects: |