One Size Does Not Fit All: The Past, Present and Future of Cystic Fibrosis Causal Therapies
Cystic fibrosis (CF) is the most common monogenic disorder, caused by mutations in the CF transmembrane conductance regulator (<i>CFTR</i>) gene. Over the last 30 years, tremendous progress has been made in understanding the molecular basis of CF and the development of treatments that ta...
| Main Authors: | , |
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| Format: | Article |
| Language: | English |
| Published: |
MDPI AG
2022-06-01
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| Series: | Cells |
| Subjects: | |
| Online Access: | https://www.mdpi.com/2073-4409/11/12/1868 |