Targeted <i>SMN</i> Exon Skipping: A Useful Control to Assess In Vitro and In Vivo Splice-Switching Studies

Targeted <i>SMN</i> Exon Skipping: A Useful Control to Assess In Vitro and In Vivo Splice-Switching Studies

The literature surrounding the use of antisense oligonucleotides continues to grow, with new disease and mechanistic applications constantly evolving. Furthermore, the discovery and advancement of novel chemistries continues to improve antisense delivery, stability and effectiveness. For each new ap...

Full description

Bibliographic Details
Main Authors: Loren L. Flynn, Chalermchai Mitrpant, Abbie Adams, Ianthe L. Pitout, Anja Stirnweiss, Sue Fletcher, Steve D. Wilton
Format: Article
Language:English
Published: MDPI AG 2021-05-01
Series:Biomedicines
Subjects:
antisense oligonucleotide
morpholino
positive control
survival motor neuron
cell penetrating peptide
Online Access:https://www.mdpi.com/2227-9059/9/5/552

Internet

https://www.mdpi.com/2227-9059/9/5/552

Similar Items