BUSULFAN-CYCLOPHOSPHAMIDE OR TREOSULFAN-FLUDARABINE-THIOTEPA-BASED MYELOABLATIVE CONDITIONING FOR CHILDREN WITH THALASSEMIA MAJOR, SINGLE CENTRE EXPERIENCE
Objective: Hemoglobinopaties are the most common genetic disorder worldwide. Patients with transfusion-dependent thalassemia major (TDT) are deficient in β-globulin chain production, resulting in ineffective erytropoiesis and hemolysis. Consequently, patients with TDT suffer from primary and seconda...
Main Authors: | , , , , , |
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Format: | Article |
Language: | English |
Published: |
Elsevier
2023-10-01
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Series: | Hematology, Transfusion and Cell Therapy |
Online Access: | http://www.sciencedirect.com/science/article/pii/S2531137923002213 |