Efficacy of CRISPR-Based Gene Editing in a Sickle Cell Disease Patient as Measured through the Eye

Sickle cell disease (SCD) exists on a phenotypic spectrum with variable genetic expressivity, making it difficult to assess an individual patient’s risk of complications at any particular point in time. Current and emerging SCD treatments, including CRISPR-based gene editing, result in a variable pr...

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Bibliographic Details
Main Authors: Alexander Pinhas, Davis B. Zhou, Oscar Otero-Marquez, Maria V. Castanos Toral, Justin V. Migacz, Jeffrey Glassberg, Richard B. Rosen, Toco Y. P. Chui
Format: Article
Language:English
Published: Hindawi Limited 2022-01-01
Series:Case Reports in Hematology
Online Access:http://dx.doi.org/10.1155/2022/6079631