Hemophilia Gene Therapy: Approaching the First Licensed Product

The clinical potential of hemophilia gene therapy has now been pursued for the past 30 years, and there is a realistic expectation that this goal will be achieved within the next couple of years with the licensing of a gene therapy product. While recent late phase clinical trials of hemophilia gene...

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Bibliographic Details
Main Authors: Paul Batty, David Lillicrap
Format: Article
Language:English
Published: Wiley 2021-03-01
Series:HemaSphere
Online Access:http://journals.lww.com/10.1097/HS9.0000000000000540