The Application of Adeno-Associated Viral Vector Gene Therapy to the Treatment of Fragile X Syndrome

Viral vector-mediated gene therapy has grown by leaps and bounds over the past several years. Although the reasons for this progress are varied, a deeper understanding of the basic biology of the viruses, the identification of new and improved versions of viral vectors, and simply the vast experienc...

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Bibliographic Details
Main Authors: David R. Hampson, Alexander W. M. Hooper, Yosuke Niibori
Format: Article
Language:English
Published: MDPI AG 2019-02-01
Series:Brain Sciences
Subjects:
Online Access:https://www.mdpi.com/2076-3425/9/2/32