Disease Modifying Therapies for the Management of Children with Spinal Muscular Atrophy (5q SMA): An Update on the Emerging Evidence
Helgi Thor Hjartarson,1 Kristofer Nathorst-Böös,1 Thomas Sejersen1,2 1Department of Neuropediatrics, Astrid Lindgren Children´s Hospital, Karolinska University Hospital, Stockholm, Sweden; 2Department of Women’s and Children’s Health, Karolinska Institute, Stockholm, SwedenCorrespondence: Thomas Sej...
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Format: | Article |
Language: | English |
Published: |
Dove Medical Press
2022-06-01
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Series: | Drug Design, Development and Therapy |
Subjects: | |
Online Access: | https://www.dovepress.com/disease-modifying-therapies-for-the-management-of-children-with-spinal-peer-reviewed-fulltext-article-DDDT |