Development of decision-making considerations to support equitable patient selection in paediatric haemophilia trials

Clinical trials for investigational haemophilia treatments such as gene therapy offer a potentially life-changing opportunity to those who are selected for enrolment. However, the number of enrolment slots available for these trials is often greatly exceeded by the number of eligible patients. Many...

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Bibliographic Details
Main Authors: Fu Anne, Strike Karen, Hamilton Korinne, Waterhouse Linda, Decker Kay, Almonte Theresa, Chan Anthony K C
Format: Article
Language:English
Published: Sciendo 2022-04-01
Series:The Journal of Haemophilia Practice
Subjects:
Online Access:https://doi.org/10.2478/jhp-2022-0007