Visual function and retinal changes after voretigene neparvovec treatment in children with biallelic RPE65-related inherited retinal dystrophy

Abstract To report quantitative retinal changes assessed by spectral-domain optical coherence tomography (SD-OCT) in children treated with voretigene neparvovec (VN) at a single center in Italy. Retrospective review of six consecutive pediatric patients with biallelic RPE65-related dystrophy treated...

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Bibliographic Details
Main Authors: Francesco Testa, Paolo Melillo, Valentina Di Iorio, Claudio Iovino, Francesco Farinaro, Marianthi Karali, Sandro Banfi, Settimio Rossi, Michele Della Corte, Francesca Simonelli
Format: Article
Language:English
Published: Nature Portfolio 2022-10-01
Series:Scientific Reports
Online Access:https://doi.org/10.1038/s41598-022-22180-6