Patient experience with acute hepatic porphyria before and after long-term givosiran treatment in a qualitative interview study

Patient experience with acute hepatic porphyria before and after long-term givosiran treatment in a qualitative interview study

Background: Acute hepatic porphyria (AHP) is characterized by debilitating and potentially life-threatening neurovisceral attacks, possible chronic symptoms, and long-term complications. In a phase 1/2 open-label extension (OLE) study and the phase 3 ENVISION study, givosiran led to sustained improv...

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Bibliographic Details
Main Authors: Hetanshi Naik, Michelle Brown, Stephen Meninger, Stephen Lombardelli
Format: Article
Language:English
Published: Elsevier 2025-03-01
Series:Molecular Genetics and Metabolism Reports
Subjects:
Acute porphyria
Attack
Chronic
Quality of life
Pain
Qualitative
Online Access:http://www.sciencedirect.com/science/article/pii/S2214426924001277

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http://www.sciencedirect.com/science/article/pii/S2214426924001277

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