Patient selection for hemophilia gene therapy: Real‐life data from a single center

Abstract Background While the number of individuals with hemophilia who are expected to be or have already been included in gene therapy trials has been regularly reported, the number of unscreened or excluded individuals, in addition to the reasons for exclusion, is mostly not reported. Methods We...

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Bibliographic Details
Main Authors: Evelien Krumb, Catherine Lambert, Cedric Hermans
Format: Article
Language:English
Published: Elsevier 2021-03-01
Series:Research and Practice in Thrombosis and Haemostasis
Subjects:
Online Access:https://doi.org/10.1002/rth2.12494