The efficacy and the safety of eltrombopag in pediatric patients with severe aplastic anemia: a systematic review

BackgroundAcquired aplastic anemia (AAA) in pediatric patients is a rare disorder characterized by hypocellular bone marrow and pancytopenia. Eltrombopag, an oral thrombopoietin receptor agonist, provides a hematologic improvement in adults with severe aplastic anemia (SAA) refractory to immunosuppr...

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Bibliographic Details
Main Authors: Maria Maddalena Marrapodi, Annamaria Mascolo, Domenico Roberti, Martina Di Martino, Concetta Rafaniello, Consiglia Riccardi, Francesca Rossi
Format: Article
Language:English
Published: Frontiers Media S.A. 2023-04-01
Series:Frontiers in Pediatrics
Subjects:
Online Access:https://www.frontiersin.org/articles/10.3389/fped.2023.1149718/full