Matched Unrelated Hematopoietic Stem Cell Transplant in Juvenile-Onset Krabbe's Disease
Background: Krabbe's disease is a neurodegenerative condition caused by a deficiency of a lysosomal enzyme, galactocerebrosidase (GALC), found mainly in the brain. There are four variants based on the age of onset: Infantile, late infantile, juvenile, and adult. Hematopoietic stem cell transpla...
Main Authors: | , , , , , |
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Format: | Article |
Language: | English |
Published: |
Wolters Kluwer Medknow Publications
2022-01-01
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Series: | Indian Pediatrics Case Reports |
Subjects: | |
Online Access: | http://www.ipcares.org/article.asp?issn=2772-5170;year=2022;volume=2;issue=3;spage=162;epage=166;aulast=Misra |