Matched Unrelated Hematopoietic Stem Cell Transplant in Juvenile-Onset Krabbe's Disease

Background: Krabbe's disease is a neurodegenerative condition caused by a deficiency of a lysosomal enzyme, galactocerebrosidase (GALC), found mainly in the brain. There are four variants based on the age of onset: Infantile, late infantile, juvenile, and adult. Hematopoietic stem cell transpla...

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Bibliographic Details
Main Authors: Ruchira Misra, Sunil Bhat, Suhani Shah, Anaita Hegde, Hiren Panwala, Divyata Hingwala
Format: Article
Language:English
Published: Wolters Kluwer Medknow Publications 2022-01-01
Series:Indian Pediatrics Case Reports
Subjects:
Online Access:http://www.ipcares.org/article.asp?issn=2772-5170;year=2022;volume=2;issue=3;spage=162;epage=166;aulast=Misra