GLP-1 receptor agonists as promising disease-modifying agents in WFS1 spectrum disorder

WFS1 spectrum disorder (WFS1-SD) is a rare monogenic neurodegenerative disorder whose cardinal symptoms are childhood-onset diabetes mellitus, optic atrophy, deafness, diabetes insipidus, and neurological signs ranging from mild to severe. The prognosis is poor as most patients die prematurely with...

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Bibliographic Details
Main Authors: Eleonora Panfili, Giulio Frontino, Maria Teresa Pallotta
Format: Article
Language:English
Published: Frontiers Media S.A. 2023-06-01
Series:Frontiers in Clinical Diabetes and Healthcare
Subjects:
Online Access:https://www.frontiersin.org/articles/10.3389/fcdhc.2023.1171091/full