GLP-1 receptor agonists as promising disease-modifying agents in WFS1 spectrum disorder
WFS1 spectrum disorder (WFS1-SD) is a rare monogenic neurodegenerative disorder whose cardinal symptoms are childhood-onset diabetes mellitus, optic atrophy, deafness, diabetes insipidus, and neurological signs ranging from mild to severe. The prognosis is poor as most patients die prematurely with...
Main Authors: | , , |
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Format: | Article |
Language: | English |
Published: |
Frontiers Media S.A.
2023-06-01
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Series: | Frontiers in Clinical Diabetes and Healthcare |
Subjects: | |
Online Access: | https://www.frontiersin.org/articles/10.3389/fcdhc.2023.1171091/full |