Efficient Gene Editing for Heart Disease via ELIP-Based CRISPR Delivery System

Liposomes as carriers for CRISPR/Cas9 complexes represent an attractive approach for cardiovascular gene therapy. A critical barrier to this approach remains the efficient delivery of CRISPR-based genetic materials into cardiomyocytes. Echogenic liposomes (ELIP) containing a fluorescein isothiocyana...

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Main Authors: Xing Yin, Romain Harmancey, Brion Frierson, Jean G. Wu, Melanie R. Moody, David D. McPherson, Shao-Ling Huang
格式: 文件
语言:English
出版: MDPI AG 2024-02-01
丛编:Pharmaceutics
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在线阅读:https://www.mdpi.com/1999-4923/16/3/343