Preferences for genetic interventions for SCA and Huntington’s disease: results of a discrete choice experiment among patients

Abstract Background Although genetic interventions are on the horizon for some polyglutamine expansion diseases, such as subtypes of spinocerebellar ataxia (SCA) and Huntington’s disease (HD), the patients’ preferences regarding these new therapies are unclear. This study aims to get insight into wh...

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Bibliographic Details
Main Authors: Nienke J.H. van Os, Mayke Oosterloo, Janneke P.C. Grutters, Brigitte A.B. Essers, Bart P.C. van de Warrenburg
Format: Article
Language:English
Published: BMC 2024-10-01
Series:Orphanet Journal of Rare Diseases
Online Access:https://doi.org/10.1186/s13023-024-03408-2