Non-ambulatory Duchenne muscular dystrophy: observations, interventions, and outcomes on a single case
Duchenne muscular dystrophy (DMD) is a X-linked recessive gene defect manifesting as a fatal, progressive neuromuscular disease. Treatment goals aim to inhibit disease progression, increase patients’ quality of life, and lengthen life expectancy. We report here a single case of non-ambulatory DMD.
Main Authors: | , , |
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Format: | Article |
Language: | English |
Published: |
Indonesian Pediatric Society Publishing House
2022
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Online Access: | https://repository.ugm.ac.id/282683/1/2447-Article%20Text-11291-2-10-20220712.pdf |