[Gene therapy for retinal dystrophies].

Genetic mutations are the cause of inherited retinal dystrophies. The underlying genetic basis of these diseases suggests that a gene therapy approach is logical either to replace or reduce the expression of defective genes. The first proof-of-concept clinical studies in patients with Leber's c...

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Bibliografische gegevens
Hoofdauteurs: Charbel Issa, P, Groppe, M, Maclaren, R
Formaat: Journal article
Taal:German
Gepubliceerd in: 2012