Gene therapy for surfactant protein B deficiency using recombinant AAV

Gene therapy for surfactant protein B deficiency using recombinant AAV

Xehetasun bibliografikoak
Egile Nagusiak:	Meyer-Berg, H, Hyde, S, Gill, D
Formatua:	Conference item
Argitaratua:	Elsevier 2019

Antzeko izenburuak

Gene therapy for surfactant protein B deficiency using recombinant AAV vectors
nork: Meyer-Berg, H
Argitaratua: (2021)

A human surfactant B deficiency air-liquid interface cell culture model suitable for gene therapy applications
nork: Munis, AM, et al.
Argitaratua: (2020)

A human surfactant B deficiency air-liquid interface cell culture model suitable for gene therapy applications
nork: Altar M. Munis, et al.
Argitaratua: (2021-03-01)

Identification of AAV serotypes for lung gene therapy in human embryonic stem cell-derived lung organoids
nork: Meyer-Berg, H, et al.
Argitaratua: (2020)

Identification of AAV serotypes for lung gene therapy in human embryonic stem cell-derived lung organoids
nork: Helena Meyer-Berg, et al.
Argitaratua: (2020-10-01)

Development of recombinant Adeno-Associated Viral vector (rAAV) for passive immunisation against ebola
nork: Tan, T, et al.
Argitaratua: (2017)

Homologous recombination mediates functional recovery of dysferlin deficiency following AAV5 gene transfer.
nork: William E Grose, et al.
Argitaratua: (2012-01-01)

Characterization of Recombinant Adeno-Associated Viruses (rAAVs) for Gene Therapy Using Orthogonal Techniques
nork: Liam Cole, et al.
Argitaratua: (2021-04-01)

Single-Step Purification/Solubilization of Recombinant Proteins: Application to Surfactant Protein B
nork: Andreas Holzinger, et al.
Argitaratua: (1996-05-01)

Efficient gene transduction in pigs and macaques with the engineered AAV vector AAV.GT5 for hemophilia B gene therapy
nork: Yuji Kashiwakura, et al.
Argitaratua: (2023-09-01)

Serotype-dependent recombinant adeno-associated vector (AAV) infection of Epstein–Barr virus-positive B-cells, towards recombinant AAV-based therapy of focal EBV + lymphoproliferative disorders
nork: Elham Ahmadi, et al.
Argitaratua: (2021-11-01)

Current Challenges and Future Directions in Recombinant AAV-Mediated Gene Therapy of Duchenne Muscular Dystrophy
nork: Shin'ichi Takeda, et al.
Argitaratua: (2013-06-01)

An AAV-Based NF-κB-Targeting Gene Therapy (rAAV-DMP-miR533) to Inflammatory Diseases
nork: Luo T, et al.
Argitaratua: (2022-06-01)

Optimized riboswitch-regulated AAV vector for VEGF-B gene therapy
nork: Reetta A. E. Eriksson, et al.
Argitaratua: (2022-12-01)

Immunogenicity and toxicity of AAV gene therapy
nork: Hildegund C. J. Ertl
Argitaratua: (2022-08-01)

AAV gene therapy vectors in the TMJ
nork: Sabine M. Brouxhon, et al.
Argitaratua: (2022-12-01)

Allometric-like scaling of AAV gene therapy for systemic protein delivery
nork: Alexandra Burr, et al.
Argitaratua: (2022-12-01)

Assessment of toxicity and biodistribution of recombinant AAV8 vector–mediated immunomodulatory gene therapy in mice with Pompe disease
nork: Gensheng Wang, et al.
Argitaratua: (2014-01-01)

Establishment of mouse model of inherited PIGO deficiency and therapeutic potential of AAV-based gene therapy
nork: Ryoko Kuwayama, et al.
Argitaratua: (2022-06-01)

Safety and efficacy of an engineered hepatotropic AAV gene therapy for ornithine transcarbamylase deficiency in cynomolgus monkeys
nork: Julien Baruteau, et al.
Argitaratua: (2021-12-01)

Probing recombinant AAV capsid integrity and genome release after thermal stress by mass photometry
nork: Eduard H.T.M. Ebberink, et al.
Argitaratua: (2024-09-01)

Variation in the surfactant protein B gene is associated with development of emphysema in alpha 1 anti-trypsin deficiency
nork: Wood, A, et al.
Argitaratua: (2007)

Lentiviral gene therapy for the treatment of ABCA3-mediated surfactant deficiency
nork: Ruffle, AR
Argitaratua: (2024)

Adding recombinant AAVs to the cancer therapeutics mix
nork: Patrick L. Mulcrone, et al.
Argitaratua: (2022-12-01)

The Role of Recombinant AAV in Precise Genome Editing
nork: Swati Bijlani, et al.
Argitaratua: (2022-01-01)

Gene Transfer in Rodent Nervous Tissue Following Hindlimb Intramuscular Delivery of Recombinant Adeno-Associated Virus Serotypes AAV2/6, AAV2/8, and AAV2/9
nork: Asad Jan, et al.
Argitaratua: (2019-11-01)

Corrigendum: Optimized riboswitch-regulated AAV vector for VEGF-B gene therapy
nork: Reetta A. E. Eriksson, et al.
Argitaratua: (2023-03-01)

Corrigendum to âAssessment of toxicity and biodistribution of recombinant AAV8 vectorâmediated immunomodulatory gene therapy in mice with Pompe diseaseâ
nork: Gensheng Wang, et al.
Argitaratua: (2015-01-01)

Editorial: Immunogenicity and toxicity of AAV gene therapy
nork: Allison Bradbury, et al.
Argitaratua: (2023-06-01)

Editorial: “AAV Gene Therapy: Immunology and Immunotherapeutics”
nork: José M. Martinez-Navio, et al.
Argitaratua: (2021-12-01)

Difficulties in the treatment of an infant survivor with inherited surfactant protein-B deficiency in Tunisia
nork: Samia Hamouda, et al.
Argitaratua: (2022-01-01)

Inclusion of PF68 surfactant improves stability of rAAV titer when passed through a surgical device used in retinal gene therapy
nork: Patrício, M, et al.
Argitaratua: (2019)

Inclusion of PF68 Surfactant Improves Stability of rAAV Titer when Passed through a Surgical Device Used in Retinal Gene Therapy
nork: Maria I. Patrício, et al.
Argitaratua: (2020-06-01)

Robust AAV Genotyping Based on Genetic Distances in Rep Gene That Are Maintained by Ubiquitous Recombination
nork: Marina I. Beloukhova, et al.
Argitaratua: (2022-05-01)

AAV-based gene replacement: The promise of gene therapy for deafness
nork: Jieyu Qi, et al.
Argitaratua: (2024-06-01)

Rational Design of AAV-rh74, AAV3B, and AAV8 with Limited Liver Targeting
nork: Christopher Chan, et al.
Argitaratua: (2023-10-01)

Optimizing an AAV-CRISPR system for retinal gene therapy
nork: Stevanovic, M
Argitaratua: (2019)

Choroideremia: molecular mechanisms and development of AAV gene therapy
nork: Patrício, M, et al.
Argitaratua: (2018)

Progress of gene therapy based on AAV inhereditary deafness
nork: Qi Jieyu, et al.
Argitaratua: (2021-06-01)

AAV for Gene Therapy in Ocular Diseases: Progress and Prospects
nork: Xiaoyu He, et al.
Argitaratua: (2023-01-01)