Systemic delivery of MicroRNA using recombinant adeno-associated virus serotype 9 to treat neuromuscular diseases in rodents

RNA interference via the endogenous miRNA pathway regulates gene expression by controlling protein synthesis through post-transcriptional gene silencing. In recent years, miRNA-mediated gene regulation has shown potential for treatment of neurological disorders caused by a toxic gain of function mec...

पूर्ण विवरण

ग्रंथसूची विवरण
मुख्य लेखकों: Pourshafie, N, Lee, P, Chen, K, Harmison, G, Bott, L, Fischbeck, K, Rinaldi, C
स्वरूप: Journal article
भाषा:English
प्रकाशित: Journal of Visualized Experiments 2018