Targeting RNA to treat neuromuscular disease.
The development of effective therapies for neuromuscular disorders such as Duchenne muscular dystrophy (DMD) is hampered by considerable challenges: skeletal muscle is the most abundant tissue in the body, and many neuromuscular disorders are multisystemic conditions. However, despite these barriers...
主要な著者: | , |
---|---|
フォーマット: | Journal article |
言語: | English |
出版事項: |
2011
|