Targeting RNA to treat neuromuscular disease.
The development of effective therapies for neuromuscular disorders such as Duchenne muscular dystrophy (DMD) is hampered by considerable challenges: skeletal muscle is the most abundant tissue in the body, and many neuromuscular disorders are multisystemic conditions. However, despite these barriers...
Κύριοι συγγραφείς: | Muntoni, F, Wood, M |
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Μορφή: | Journal article |
Γλώσσα: | English |
Έκδοση: |
2011
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Παρόμοια τεκμήρια
Παρόμοια τεκμήρια
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Syncoilin expression in neuromuscular disorders
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Syncoilin expression in neuromuscular disorders.
ανά: Howman, E, κ.ά.
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