Targeting RNA to treat neuromuscular disease.

The development of effective therapies for neuromuscular disorders such as Duchenne muscular dystrophy (DMD) is hampered by considerable challenges: skeletal muscle is the most abundant tissue in the body, and many neuromuscular disorders are multisystemic conditions. However, despite these barriers...

תיאור מלא

מידע ביבליוגרפי
Main Authors: Muntoni, F, Wood, M
פורמט: Journal article
שפה:English
יצא לאור: 2011